BioTech Mag Search: Gene Therapy
Improving the on-target activity of high-fidelity Cas9 editors by combining rational design and random mutagenesis
Abstract Genomic and post-genomic editors based on CRISPR/Cas systems are widely used in basic research and applied sciences, including human gene therapy. Most genome editing...
11 hours ago - Springer
RG6501 Phase 1/2a Clinical Results to Be Presented at 2023 Retinal Cell and Gene Therapy Innovation Summit
CARLSBAD, Calif.--- $LCTX LineageCellTherapeutics-Lineage Cell Therapeutics, Inc. , a clinical-stage biotechnology company developing allogeneic cell therapies for unmet...
2 days ago - San Diego Biotechnology
Maltese Patient Received World's First ND1-LHON Gene Therapy Injection Donated by Neurophth in China
WUHAN, China and SAN DIEGO, March 7, 2023 /PRNewswire/ - Matthias Szabo Zarb, a Maltese college student, was diagnosed with Leber hereditary optic neuropathy caused by ND1...
15 days ago - San Diego Biotechnology
EU approves Hemgenix, one-time gene therapy for hemophilia B
Posted on: 7 March 2023, The European Commission has conditionally approved Hemgenix , a one-time gene therapy to treat adults with hemophilia B. Hemgenix, originally...
15 days ago - Gene Therapy
NEW?* PROGRAM MANAGER - CELL AND GENE THERAPY - PharmaScouts - La Jolla, CA
The consortium is advancing development of these new technologies in a non-competitive environment, establishing best practices and standards for a...
16 days ago - San Diego Biotechnology
Assoc Director, QA - Gene Therapy Manufacturing - Insmed Incorporated - San Diego, CA
Highly organized with a strong attention to detail, clarity, accuracy and conciseness. Perform audits, write reports and follow up on...
22 days ago - San Diego Biotechnology - 4 articles
Gene therapy startup Locanabio lays off staff, narrows focus on Duchenne
Biotech startup Locanabio has laid off 30% of its workforce, portending a limited scope going forward for the gene therapy developer, backed with more than $150 million since...
26 days ago - San Diego Biotechnology
Commercialization of Gene Therapy is coming soon: Neurophth Completes Patient Enrollment for Phase III clinical trial for the gene therapy treatment of LHON
WUHAN, China and SAN DIEGO, Feb. 21, 2023 /PRNewswire/ - Neurophth Therapeutics, Inc. announced today that the last patient has been enrolled in the Phase III clinical trial...
1 month ago - San Diego Biotechnology
FDA officials offer advice on gene therapy trials
Posted on: 9 February 2023, Officials from the US Food and Drug Administration's Center for Biologics Evaluation and Research Office of Tissues and Advanced Therapies asserted...
1 month ago - Gene Therapy
Novel opto-fluidic drug delivery system for efficient cellular transfection
Intracellular drug delivery is at the heart of many diagnosis procedures and a key step in gene therapy. Research has been conducted to bypass cell barriers for controlled...
1 month ago - Journal of Nanobiotechnology
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2nd International Conference on Generic Drugs and Biosimilars
2nd International Conference on Generic Drugs and Biosimilars
2nd International Conference on Generic Drugs and Biosimilars
2nd International Conference on Generic Drugs and Biosimilars
New UN Report: Limiting Global Warming to 1.5 Degrees Celsius Requires Deep...
Ionis accounces FDA advisory committee voted unanimously for a potential...
If approved, tofersen will be the first treatment targeting a genetic cause of ALS and the next marketed Ionis-discovered antisense medicine FDA decision expected by April 25...
Director/Senior Director, Human Resources - Recludix Pharma - San Diego, CA
Identify innovative solutions and compelling training to support Recludix employees' leadership and professional growth. $180,000 - $220,000 a yearFrom Recludix...
Sr. Research Scientist I, Formulation Process Development - Gilead Sciences...
Lead the design and execution of development studies that employ a variety of analytical techniques, including HPLC, capillary electrophoresis, spectroscopy,...
School of Medicine Student on Finding Love as a Trans Woman
Like most people her age, Daniella McDonald spent a lot of time talking with friends about relationships and using dating apps. But, as a transgender woman, the experience for...
DrTalks Presents The Reverse Inflammaging Body and Mind Longevity Medicine...
CARLSBAD, Calif., March 22, 2023 /PRNewswire/ - DrTalks.com is pleased to announce the upcoming Reverse Inflammaging Body and Mind Longevity Medicine Summit from April 25th to...
Active targeting schemes for nano-drug delivery systems in osteosarcoma...
Osteosarcoma, the most common malignant tumor of the bone, seriously influences people's lives and increases their economic burden. Conventional chemotherapy drugs achieve...
UFGI Faculty Spotlight - Looking at Human Neurological Disorders through...
Observing group-living animals with drones and computer vision
A drone is flying over a herd of plains zebras in central Kenya. It is flying quite high so that the animals are not bothered by it. These zebras are really interesting for...
New method shrinks 3D images of cells for faster storage and retrieval
Single-cell analysis is a powerful biomedical technique used in various fields of biology and medicine to identify rare cell populations, track cell development and...