• New gene-delivering workhorse could make gene therapy safer, more effective for muscle diseases

    25 days ago - By Gene Therapy

    Posted on: 13 September 2021,
    Genetic muscle diseases lead to progressive muscle wasting and often early death, with few treatment options and no cure. Some gene therapies that use a harmless virus to deliver a functioning copy of a disease-causing gene to cells have shown promise in clinical trials for a subset of muscular dystrophies, but have faced challenges. High doses of the gene-carrying virus are needed to reach the muscles throughout the body and the viruses used in these trials often end up in the liver more than in the muscle. This has led to high levels of the virus in the...
    Read more ...

     

  • Gene found in monkeys and mice could work as a new type of antiviral to block HIV, Ebola, and other deadly viruses in humans

    25 days ago - By ScienceDaily

    A nationwide team of researchers has determined how a genetic mutation found in mice and monkeys interferes with viruses such as HIV and Ebola. They say the finding could eventually lead to the development of medical interventions in humans.
    Read more ...