• Test of adeno-associated viral vectors with gene therapy in dogs with hemophilia produces evidence of genomic changes

    11 days ago - By Phys

    A team of researchers from Children's Hospital of Philadelphia, the University of Pennsylvania, the University of North Carolina at Chapel Hill and Johns Hopkins School of Medicine has found evidence of genomic changes in dogs that were part of a long-term test of the use of adeno-associated viral vectors in gene therapy. In their paper published in the journal Nature Biotechnology, the group describes their 10-year study of the gene therapy technique in dogs and what they learned from it. Charles Venditti with the U.S. National Institutes of Health has published a News and Views piece...
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